For You (Yes, YOU!)

Dear Fans, I wanted to send a message to say Thank You for your support! Some of you support me by visiting this website, coming to Ryan’s Day, sharing posts on facebook, & commenting to keep the message going. Encourage others and be an Inspiration to the world. Stay positive and never lose hope... My [...]

November 5th, 2015|Wheelz Blog|

Moms, Regulators, Biotech Startups, and the Battle Over a Potentially Life-Saving Drug

By Paul M. Barrett October 30, 2014 - Published via Bloomberg Business The 2014 World Cup elevated soccer to the top of Aidan Leffler’s roster of obsessions, rivaled only by endangered big cats—especially jaguars, “the coolest”—and Star Wars spaceships. In recognition of his new interest, he’s set up a miniature soccer field with 4-foot-wide goals in [...]

February 16th, 2015|Wheelz Blog|

UPDATE: DMD: Encouraging Results for SMT C1100!

Great News! A phase 1b trial of a drug designed to increase utrophin protein levels in Duchenne MD-affected muscles, appears safe and may have muscle-protective effects.   Article Highlights: SMT C1100, an experimental drug designed to treat Duchenne and possibly Becker MD by raising utrophin protein levels in mature muscles, has shown encouraging results in [...]

October 13th, 2014|Wheelz Blog|

LATEST NEWS! AND IT’S GOOD!

MDA-Supported Summit reports positive data on its Utrophin Modulation Program for the treatment of DMD Summit PLC, developer of experimental Duchenne muscular dystrophy drug SMT C1100, announced additional encouraging findings regarding this drug's apparent effects on DMD-affected muscles. In an October 8, 2014 press release, Summit reported: C1100 was safe and well tolerated at all doses [...]

October 10th, 2014|Wheelz Blog|

“My Humble Speech For A Great Young Man” by Noemi Craib

Texas Comission on Environmental Quality Contract Specialist Noemi L. Craib wears many hats.  She not only works to improve our local air quality, but Craib also devotes time to improving her public speaking skills through Toastmasters.  Prior to this past Christmas holiday, Noemi gave a beautiful presentation on Wheelz, his Music, and Duchenne Muscular Dystrophy...."My [...]

January 7th, 2014|Wheelz Blog|

“Searching” Video by Wheelz featuring “Twon

August 21st, 2013|Wheelz Blog|

CBS News: DMD, The Most Common of The Rare Diseases

With an incidence of 1 out of 3,500 male births, Duchenne muscular dystrophy is one of the most common of the orphan or rare diseases. But, the effects of the disease, which causes death by the average age of 25, are some of the most destructive according to experts. Orphan or rare diseases are defined [...]

March 5th, 2013|Wheelz Blog|

Quantum Leap in Gene Therapy of Duchenne Muscular Dystrophy

Quantum Leap in Gene Therapy of DMD Jan. 15, 2013 — Usually, results from a new study help scientists inch their way toward an answer whether they are battling a health problem or are on the verge of a technological breakthrough. Once in a while, those results give them a giant leap forward. In a [...]

January 24th, 2013|Wheelz Blog|

Dantrolene: Already Approved by the FDA, Looks Promising

UCLA scientists find drug that may help fight Duchenne muscular dystrophy Drugs are currently being tested that show promise in treating patients with Duchenne muscular dystrophy (DMD), an inherited disease that affects about one in 3,600 boys and results in muscle degeneration and, eventually, death. Now, scientists at UCLA have found a drug, already approved [...]

January 4th, 2013|Wheelz Blog|

Boys Helping Boys: Meet Tyler Armstrong

Tyler Armstrong: Climbing for a Cure! 8-year-old Tyler Armstrong climbed to the top of Mt. Kilimanjaro to benefit CureDuchenne. He climbed to raise awareness and funds to find a cure for Duchenne muscular dystrophy. Tyler climbed for the 300,000 Duchenne boys around the world who can't climb. To donate, go to www.topwithtyler.com. For more information, [...]

December 5th, 2012|Wheelz Blog|